[1/3/2025] Gene and Cell Therapy- weekly digest from PackGene

Featured

• Dec 31 | The Biggest Medical Advances of 2024: Transforming Lives read more ?
• Dec 30 | Precigen Completes Submission of BLA with Request for Priority Review to the FDA for PRGN-2012 for the Treatment of Adults with Recurrent Respiratory Papillomatosis read more ?

News

• Dec 31 | A Look at 2024's Patent Expirations and Generic Competition read more ?
• Dec 31 | Pfizer ends work on Sangamo's hemophilia gene therapy, crushing biotech's hopes read more ?
• Dec 30 | NLS Pharmaceutics Ltd. and Kadimastem Ltd. Announce Filing of F-4 Registration Statement with the SEC Ahead of Proposed Merger read more ?
• Dec 30 | CARsgen Announces Positive Topline Results from China GC/GEJ Pivotal Phase II Clinical Trial of Claudin18.2 CAR-T (Satri-cel) read more ?
• Dec 26 | AusperBio Secures $73 Million in Series B Financing to Advance Functional Cure for Chronic Hepatitis B read more ?

Articles

• Dec 31 | Heterogeneity, a weak link between constrained dose of AAV and long-term efficacy of gene therapy to muscular dystrophy: A critical review and prospective analysis. read more ?
• Dec 31 | Angiotensin‐converting enzyme 2 modulation of pyroptosis pathway in traumatic brain injury: A potential therapeutic target read more ?
• Dec 30 | Recent developments in translational imaging of in vivo gene therapy outcomes read more ?
• Dec 30 | Autologous transplantation of mitochondria/rAAV IGF-I platforms in human osteoarthritic articular chondrocytes as a novel therapeutic concept for human osteoarthritis read more ?
• Dec 26 | Heat acclimation in mice requires preoptic BDNF neurons and postsynaptic potentiation read more ?
• Dec 26 | Interlaboratory Measurement of Adeno-Associated Virus: Comparative Quantification of Full and Empty Capsids read more ?