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We’re thrilled to participate in the annual?ADVANCE?Sanfilippo Community Conference, hosted by the Cure Sanfilippo Foundation. The ADVANCE event gathers experts for collaboration, knowledge sharing, and focused?learning on?#Sanfilippo. This?year, our own Dr. Heather Lau MD MS, Executive Director of Global Clinical Development, gave an important presentation on the significance of the accelerated approval process for Sanfilippo patients and their families.?? ? Our partnership with the Sanfilippo community is vital to everything we do. Thank you, Heather and team, for representing us! ? Link to?Cure?Sanfilippo:?https://lnkd.in/eb2k93T

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Roberto Giugliani

Professor, Dep Genetics, UFRGS - Founder and Member, Med Genet Serv, HCPA - Co-President, House of Rares - Head, Rare Diseases, DASA-GENEONE - Member, Brazilian Academy of Sciences

4 个月

I am very pleased to hear that we are moving forward in the treatment of Sanfilippo disease, a major need in the MPS field.

Anne Brandon, BSN, RN, LNCC, RCL

7 Time President’s Club Award Winning Patient Diagnosis Liaison @ Ultragenyx | Legal Nurse Consultant, Certified, Regional Clinical Liaison, Certified

4 个月

Thanks for sharing

Mark Kryah, BS ChE, PMP

Executive Director/Program Team Leader, Ultragenyx Pharmaceutical Inc.

4 个月

Way to represent Heather!!!

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