New research from AstraZeneca in Nature Portfolio demonstrates the transformative potential for gene editing to transform outcomes for people living with rare genetic disorders by addressing their underlying causes. ? The new gene editing tool showed enhanced precision to correct genetic mutations, while reducing off-target effects. ? This advancement could help accelerate potential new treatments for a range of diseases, including rare conditions—of which 80% are believed to have a genetic cause. ? Learn more here: https://lnkd.in/eWkEhvVk
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2 天前This is a remarkable leap forward for medical science and for the future of treating rare genetic disorders. The precision and reduced off-target effects showcased here bring hope for transforming lives by targeting the root causes of these conditions. Kudos to AstraZeneca and Alexion for pioneering research that holds such promise for those affected by genetic diseases!