X4 Pharmaceuticals

Jennifer has lived with WHIM syndrome her entire life, but until just a decade ago didn’t know the name of her condition. Now in her sixties, and after multiple tests that made her feel like a “science experiment,” she finally knows the reason behind her unexplained and chronic infections. Read her story in this Patient Worthy piece: https://bit.ly/4eKMAS9 ? We are grateful for and inspired by Jennifer’s words and working hard to ensure that her diagnostic journey becomes the exception rather than the rule for those living with rare diseases such as WHIM syndrome.

Coming up this month: We’re focused on #WHIMsyndrome at multiple industry events. At #AMCPNexus, X4 is leading encore presentations of data from our Phase 3 open-label extension (OLE) and sharing neutrophil and lymphocyte data in WHIM syndrome at #ESID2024, as well as connecting with healthcare providers to discuss this rare #immunodeficiency at #IgNS2024.

ICYMI: September kicked off the investor conference season, including Cantor Fitzgerald's Global Healthcare Conference where our CFO Adam Mostafa outlined our plans for the US launch of the first approved product in WHIM syndrome and to advance our newly initiated pivotal Phase 3 clinical trial for a potential second indication in chronic neutropenia. Catch the replay here: https://bit.ly/3XVxXoC #CantorHCC

Last week we attended Life Science Cares Boston’s Mini Golf for Good Tournament in Technology Square! The event supports LSC’s nonprofit partners who are each dedicated to ending poverty across Greater Boston. As a Boston-based company, we appreciate the opportunity to join our fellow members of the #biotech community to support such an important cause.

Here at the North American Immuno-Hematology Clinical Education and Research (NICER) 2024 Symposium we have been proud to share our mission to help address unmet needs for people living with rare immunodeficiencies like WHIM syndrome—a distinct, diagnosable, and treatable condition. Learn more about an FDA-approved treatment at https://bit.ly/4daZLeh #WHIMsyndrome #immunology #hematology #raredisease #immunodeficiency?

X4 is proud to sponsor Path4Ward, a physician-initiated no-cost genetic testing program, to help remove barriers to timely diagnosis of rare immunodeficiencies like WHIM syndrome. We are at the North American Immuno-Hematology Clinical Education and Research (NICER) 2024 Symposium discussing the critical role of genetic testing in informing WHIM syndrome diagnosis. Find more information about no-cost genetic testing at https://bit.ly/3XvQs3N #NICER2024 #WHIMsyndrome #immunology #hematology #raredisease #genetictesting?

Left undiagnosed, WHIM syndrome can lead to life-threatening complications, but disease heterogeneity can delay diagnosis. This week, X4 is at the North American Immuno-Hematology Clinical Education and Research (NICER) 2024 Symposium talking with immunologists and hematologists to raise awareness of this rare combined primary immunodeficiency. Diagnose early by learning when to suspect WHIM syndrome at https://bit.ly/4efVKpP #NICER2024 #WHIMsyndrome #immunology #hematology #raredisease #immunodeficiency?

Find us at #immunology conferences this month! Check out encore presentations of data from our Phase 3 open-label extension (OLE) in #WHIMsyndrome at the Consortium of Independent Immunology Clinics (CIIC) Fall Conference and the North American Immuno-Hematology Clinical Education and Research (NICER) Symposium. Looking forward to connecting with the #immunology community about a new treatment option for this rare combined primary immunodeficiency. #CIICFall2024 #NICER2024

This Saturday found us out in force supporting the primary #immunodeficiency community at the #FranklinParkZoo for the Immune Deficiency Foundation Boston #WalkForPI. As we work hard to deliver better solutions for people with rare and life-limiting #primaryimmunodeficiencies such as chronic #neutropenia and #WHIM syndrome, we will keep engaging with and learning from the individuals and families we are committed to serving.

Did you know? Nearly 500 genetic defects are known to cause inborn errors of immunity, also known as primary immunodeficiencies. Some may cause neutropenia, meaning a reduced number of neutrophils in the blood. Free genetic testing is available. Learn more at https://bit.ly/3AE3TG4.