World Orphan Drug Congress USA

We're officially just 6 weeks away from the world's leading Orphan Drug and rare disease event! ?? ?????? ???????????? ?????? ?????????? ???????????? ???????? ???????????????? ?????? ????????? ? Discover the latest research & technologies on our sold out expo floor ? Meet with the largest gathering of pharma & biotech powerhouses ? [NEW] 'Speed dating' networking event for quick, valuable connections ? Keynotes from top industry experts ? Featured presentations across 10 track stages ? Engage in interactive panels, roundtable discussions & 1-to-1 meetings ? Develop you professional network & find your next partner and MORE. ??????'?? ??????????????????? The National Institutes of Health (NIH),?Thermo Fisher Scientific,?Biotechnology Innovation Organization (BIO), FDA, Ovid Therapeutics, Sanofi,?Boston Children's Hospital,?Muscular Dystrophy Association, Amgen, NBC News, Rhythm Pharmaceuticals Inc.,?Alexion Pharmaceuticals, Inc.,?Merck, BBC StoryWorks, Pfizer, The ALS Association,?EUCOPE - European Confederation of Pharmaceutical Entrepreneurs,?and so many more! ? Secure your spot today ? ????% ?????? ??????????-???????? ?????????????? (savings expire this Friday, March 14): https://lnkd.in/eaz-cxwZ ?????????????????????????? ?????? ???????????? ?????? ?????????????? ?????????????????? & ???????????????? ?????????????????????????? (less than 100 still available): https://lnkd.in/ezqcD2G4 #WorldOrphanUSA ??? April 22-24 ?? Boston Convention & Exhibition Center #RareDisease #OrphanDrugs

Honored to be moderating a panel on this timely topic at World Orphan Drug Congress USA. Looking forward to an engaging discussion with this group of seasoned industry executives. Ted Slocomb Douglas Paul Amanda Forys Jim Coccia

We are thrilled to welcome the Biotechnology Innovation Organization (BIO) as a Supporting Partner of the World Orphan Drug Congress USA 2025! BIO is the world’s largest advocacy association representing the biotechnology sector. Our members range from entrepreneurial start-ups developing their first product to Fortune 500 multinationals, and includes state biotechnology associations, whose leadership at the local level is crucial to building a global biotechnology ecosystem. ???? BIO members are involved in the research and development of innovative biopharmaceutical, agricultural, industrial and environmental biotechnology products. BIO also produces the?BIO International Convention, the world’s largest gathering of the biotechnology industry, which will be held in Boston, June 16th – 19th, 2025. Meet the BIO team this April 22-24 in Boston and learn about their crucial role in advancing #raredisease innovation and policies. Catch Michele Oshman, BIO's ?????????? ?????????????? ???????????????? & ????????, ?????????????? ???????????????? ???????????? ???? ?????????????????????and Dr. Karin Hoelzer, BIO’s ???????????? ???????????????? ?????? ?????????????? ????????????????, on the #WorldOrphanUSA Keynote stage ? hear from Melody Calkins, BIO’s ???????????????? ???? ???????????????????? ????????????, chairing the?Payers & HTA?and?Pricing & Reimbursements?track stages on day 2. ??? ??? Join the conversation as BIO drives key discussions on policy, #patientadvocacy, reimbursement and advancing the ecosystem to shape current and future #orphandrug development. Don’t miss out – our ????% ??????????-???????? ???????????????? ?????????????? ???????? ????????????! Secure your spot below and join industry leaders reimagining the future for patients living with a #raredisease. Book your tickets today ? https://lnkd.in/eaz-cxwZ Patient advocates & hospital practitioners, secure one of the few remaining free VIP passes now ? https://lnkd.in/ezqcD2G4 Learn more about BIO here ??www.BIO.org #WorldOrphanUSA #IamBIOtech

After great meetings at BIOTECanada Investment Summit, Whistler BC Canada, our VP Preclinical Development & Regulatory Affairs, Marie-Eve Bordeleau, Ph.D. will attend World Orphan Drug Congress USA in Boston on April 22-24. Please feel free to connect with her !

?? As we celebrate?#InternationalWomensDay this week, we want to highlight some of the incredible?women shaping the future of the #orphandrug and #raredisease space who will be taking the World Orphan Drug Congress USA 2025 stage next month, including... ?? Maha Radhakrishnan,?Executive Partner,?Sofinnova Investments ?? Anne Bechet, Global Head of Clinical Development and General Manager, JCR Pharmaceuticals ?? Michele Oshman, Chief Patient Advocate & Head, Patient Advocacy Center of Excellence,?Biotechnology Innovation Organization ?? Effie Parks, Podcast, Host, Director of Partnerships, Once Upon a Gene Podcast ?? Ella Balasa, Patient Engagement Consultant,?Patient Advocate ?? Lindsay Reel, VP, Pharmacy Practice & Specialty Solutions,?EVERSANA ...?????? ???????? ????????! Their expertise and dedication are driving?scientific breakthroughs, patient advocacy, and regulatory advancements – making a profound impact on the lives of those affected by rare diseases. ?????? Join these incredible women and hundreds of industry leaders next month at the world's most important orphan drug and rare disease event. ???????????? ???????? ???????????? ?????????? ???????????? ?????? ??????????-???????? ???????????????? ?????????????? ?????? ???????????? ??????????. Book 20% off ?? https://lnkd.in/eaz-cxwZ Patient advocates & hospital practitioners, secure your complimentary VIP pass today (???????? ???????? 100 ???????????? ?????????? ??????????????????) ?? https://lnkd.in/ezqcD2G4 #WorldOrphanUSA April 22-24 Boston Convention & Exhibition Center

? A panel you won't want to miss for World Orphan Drug Congress USA ? In this panel, patient advocates, caregivers, and community leaders will discuss the special sauce. This panel will leave you with actionable, tangible take-aways to improve therapeutic development, strengthen pipelines, build patient-driven company cultures, impact patients in need of treatment, and efficiently meet business goals through authentic and powerful patient partnerships. ?? Mike Porath ?? Luke Rosen ?? Dionne L. Stalling ??Seth Rotberg, MNM ?? Mackenzie Abramson, MPH View the full agenda here:https://lnkd.in/e8_HKgJs #Raredisease #WorldOrphanUSA

Meet our Supporting Partner ? The Alliance for Regenerative Medicine (ARM) – a leading international advocacy organization championing the benefits of engineered cell therapies and genetic medicines for patients, healthcare systems, and society. ???? ?? As a community, ARM builds the future of medicine by convening the sector, facilitating influential exchanges on policies and practices, and advancing the narrative with data and analysis. They actively engage key stakeholders to enable the development of #advancedtherapies and to modernize healthcare systems so that patients benefit from durable, potentially curative treatments. ?? ??? As the global voice of the sector, ARM represent more than 400 members across 25 countries, including emerging and established biotechnology companies, academic and medical research institutions, and patient organizations. Catch ARM's very own Chief Executive Officer, Tim Hunt, on the World Orphan Drug Congress USA 2025 Keynote stage in the panel discussion – ???????????????? ?????? ??????????????????: ?? ??????????????????????, ??????????????????, ?????? ?????????????????? ???????????????? ?????? ???????????? ??????????.???? Don't miss your chance to join the conversation! ???????? ???? ???????? ???????????????????????? ??????????. 20% off early-bird tickets ? https://lnkd.in/eaz-cxwZ Free VIP passes for patient advocates & HCPs (less than 100 still available) ? https://lnkd.in/ezqcD2G4 #WorldOrphanUSA April 22-24 Boston Convention & Exhibition Center #RareDisease #OrphanDrugs #CellTherapies #GeneticMedicine #PatientAdvocacy

With all the action happening in Boston this April at the World Orphan Drug Congress USA 2025, you need a comfortable, convenient, and discounted place to stay. ??? ?? Don't worry we've got you covered! Secure your stay through our room block, exclusive to #WorldOrphanUSA 2025 attendees. Act now – our ???????? ?????????? ???? ????% ????????! ?? Book your hotel room today: https://lnkd.in/gEbZdRex ?????? ???????? ?????????????? ?????? ???????? ??????????? ? ? Receive an ?????????????????? ???????????????????? ???????? on your stay ? Conveniently connected to the Boston Convention & Exhibition Center – ???????? ?? ?????? ???????????? (????????????!) ???????? ???? ?????? ?????????? ? Majority of attendees will be staying there – making it ???????????????????? ???? ???????? ???????? ?????? ???????? ???????? ???????????? *???? ?????? ???????? ?????? ?????????????????? ?????????????????? ?????? ?????????????????????? ??????????, ???????????? ?????????????? ?????? ?????????? ????????????????.

New Gold Sponsor announcement! ?? Join us in welcoming ERGOMED, a full-service, global Phase I-IV clinical development and trial management service partner with leading expertise in developing oncology and rare disease drugs, to the World Orphan Drug Congress USA 2025! Founded in 1997, Ergomed’s proven delivery record, expertise, and true partnership means their sponsors can trust us to deliver their oncology trials, whatever the challenge. They also offer an industry-leading suite of specialist pharmacovigilance (PV) solutions under the PrimeVigilance brand. Ergomed has supported and managed clinical development, trial management, pharmacovigilance, and medical information services for over 300 clients in more than 100 countries. ??? ?? Meet the Ergomed team in just 7 weeks at #WorldOrphanUSA learn more! Plus, catch our Gold Sponsor's very own Senior VP Strategic Solutions and Patient Centricity and Director of Patient Engagement on stage, April 23. ??? ??????????-???????? ?????????????? ?????? ?????? ????% ??????.?Don’t miss your chance to connect with industry leaders at the premier event for #raredisease and #orphandrug innovation. Register now & save??? https://lnkd.in/eaz-cxwZ FREE passes for patient advocates & HCPs available here??? https://lnkd.in/ezqcD2G4 ?????????? ????????: April 22-24 ??????????: Boston Convention & Exhibition Center

?? We’re excited to highlight an insightful Presentation from our very own Gold Sponsor, Genome Medical – coming to the #WorldOrphanUSA 2025?Diagnosis & Drug Discovery track stage April 24 ? ???????????????????????? –?"???????????????? ?????? ??????: ???????????????????????? ???????? ?????????????? ???????????????? ?????????? ?????????????????????? ?????????????? ????????????????????????" ???Sara Riordan, MS, CGC, Vice President, Strategy, Genome Medical ???Natalie M. Beck, MGC, CGC, Senior Manager, Clinical Trials and RWD, Genome Medical This session will explore how?telegenetics?is transforming access to rare disease clinical trials, breaking down barriers for patients, and accelerating the path to new treatments. Don’t miss this opportunity to learn from leading experts in genomic medicine – ???????????? ???????? ???????? ??????????! ? ???????? ????% ?????? ??????????-???????? ?????????????? ??? https://lnkd.in/eaz-cxwZ Free passes for patient advocates and hospital practitioners are selling out fast. ? ???????????? ?????????? ?????????? ????https://lnkd.in/ezqcD2G4 #WorldOrphanUSA April 22-24 Boston Convention & Exhibition Center #RareDisease #OrphanDrugs #Telegentics #GenomicMedicine #ClinicalTrails #PatientCare