Solid Biosciences

Solid Biosciences, which acquired UF Innovate | Accelerate startup AavantiBio, Inc., is breaking new ground in the fight against Duchenne muscular dystrophy! ??? Solid Biosciences recently shared exciting updates on their INSPIRE DUCHENNE clinical trial for SGT-003, an advanced AAV micro-dystrophin gene therapy candidate. The trial is expanding to include 43 participants and is now open to children aged 4 to under 12 years old. They’ve also extended the assessment period from 12 to 18 months, which will provide deeper insights on how well SGT-003 can slow disease progression. With three new trial sites and initial data expected in early 2025, the future looks bright for #Duchenne treatment. We are so incredibly proud of our startups for pushing the boundaries of medical innovation and advancing critical treatments that change lives! #OrigiGator #UFnews

Solid is a proud sponsor of the John Walton Muscular Dystrophy Research Centre 10-Year Anniversary Event ‘Neuromuscular Diseases: the next 10 years’ taking place November 24-25, in Newcastle, UK. Congratulations on this milestone and for advancing care and research for the neuromuscular community, John Walton Muscular Dystrophy Research Centre @ Newcastle University. For more details, and to check out the full agenda, visit: https://lnkd.in/g_zSkKAr ? #JWMDRC #NeuromuscularResearch

Join us tomorrow at 1 PM ET for our free webinar with Jett Foundation! We will be sharing updates on the INSPIRE DUCHENNE clinical trial for SGT-003, a next-generation microdystrophin gene therapy for individuals living with Duchenne muscular dystrophy. Register here: https://lnkd.in/epBSAjeg #JettFoundation #DuchenneMuscularDystrophy #DuchenneAwareness #RareDiseaseResearch

Tune into the latest webinar from Solid Biosciences hosted by Defeat Duchenne Canada. ?? Solid Biosciences shared exciting news: enrollment for their SGT-003 trial will begin soon at SickKids in Toronto. With Health Canada’s approval, they expect to start in Q4 2024, enrolling two cohorts of children with #Duchenne #musculardystrophy ages 4 to 12. All participants will receive SGT-003 and be monitored for five years. Get the details: https://bit.ly/3Y2ttfA

Bo Cumbo, President & CEO, and Gabriel Brooks, M.D., CMO, will be presenting at the Jefferies London Healthcare Conference on Wednesday, November 20, at 1:30 PM GMT/8:30 AM ET. Tune into the live fireside chat on our Events page: https://lnkd.in/eJXs83j? ?? #GeneticMedicine #JefferiesHealthcare #CardiacDisease #NeuromuscularDiseases

Solid Biosciences joined PPMD earlier this week for a community webinar to provide an update on the INSPIRE DUCHENNE clinical trial for SGT-003, a next-generation microdystrophin gene therapy for individuals living with Duchenne. Included in the update were details about the current progress in the study, the company’s efforts underway to expand eligibility criteria and participating clinical trial sites, and a Q&A portion with the community. Watch the recording: https://lnkd.in/eDs3EdvX

Our VP, Patient Advocacy?Annie Ganot, and our VP, R&D?Sharon McGonigle, will speak at the Ladders to Cures event “Accelerating Gene Therapy Clinical Trials in Seropositive Patients” at the?Broad Institute of MIT and Harvard?tomorrow, November 14. ? From 9:15-9:30 AM ET, Annie will share her personal journey advocating for patients living with Duchenne muscular dystrophy and navigating the additional obstacles that AAV seropositive patients face.? ? Sharon will present from 11:00-11:15 AM ET and will also participate on a panel from 11:45 AM-12:30 PM ET to discuss the challenges posed by AAV antibody models and measurements. ? Register to attend virtually or in person:?https://lnkd.in/g37-pHdq ? #AAVImmunology #GeneTherapy #PatientAdvocacy #Duchenne?

Join us on Wednesday, November 13 at 1 PM ET for our free webinar with Defeat Duchenne Canada: INSPIRE DUCHENNE Community Update The Solid team will provide the latest information on the INSPIRE DUCHENNE clinical trial for SGT-003, a next-generation microdystrophin gene therapy for individuals living with Duchenne muscular dystrophy. Register today: https://lnkd.in/e-ZF3mEe #DuchenneMuscularDystrophy #DuchenneAwareness #RareDiseaseResearch

Join us tomorrow, November 12 at 1 PM ET for a free community webinar “INSPIRE DUCHENNE Clinical Trial Update and Study Expansion”?with Parent Project Muscular Dystrophy. We will provide an update on the INSPIRE DUCHENNE clinical trial for SGT-003, a next-generation microdystrophin gene therapy for #Duchenne, and will be answering questions from the community. Register and submit questions ahead of the discussion here: https://lnkd.in/ekBKj9K4 #DuchenneMuscularDystrophy #DuchenneAwareness #RareDiseaseResearch

Solid is a proud sponsor of Little Steps Duchenne-Becker Muscular Dystrophy Bi-Annual Conference, taking place Tuesday, November 12. This important event will bring together families, physicians, healthcare professionals, researchers, and industry leaders to collaborate and improve the quality of life for those affected by Duchenne and Becker muscular dystrophy in Israel. To learn more and register, visit: https://lnkd.in/esc2WfPg Little Steps Association for Duchenne and Becker Muscular Dystrophy patients #DuchenneMuscularDystrophy #DuchenneAwareness