Happy #RareDiseaseDay! To #LightUpForRare, our PepGen pioneers created a string of lights with how they shine a light on rare disease. The string of lights helps to remind us why we strive to improve the lives of people with rare neuromuscular disorders.
PepGen
生物技术研究
Boston,Massachusetts 11,070 位关注者
Better Technology. Better Delivery. Developing a new generation of disease-modifying therapies.
关于我们
Driven by our proprietary Enhanced Delivery Oligonucleotide (EDO) platform, we are creating a pipeline of disease-modifying therapeutics with the potential to safely and effectively target the root cause of serious genetic neuromuscular and neurological disorders.
- 网站
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https://pepgen.com
PepGen的外部链接
- 所属行业
- 生物技术研究
- 规模
- 51-200 人
- 总部
- Boston,Massachusetts
- 类型
- 上市公司
- 创立
- 2018
- 领域
- Biotechnology、Chemistry、Biology、Bioscience、Life sciences和Therapeutics
地点
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主要
321 Harrison Ave
8th Floor
US,Massachusetts,Boston,02118
PepGen员工
动态
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Our conference call on our initial DM1 FREEDOM data reported this morning will begin at 8 am ET. We invite you to join the webcast here: https://lnkd.in/eu6nM_kr
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Alongside our promising DM1 results, we also shared our financial results for the fourth quarter and year-end 2024 and recent corporate highlights. Learn more: https://lnkd.in/eGTRSpra
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We are excited to share initial data from our FREEDOM-DM1 trial in patients with #DM1. Robust splicing correction after only a single dose, along with a favorable emerging safety profile, were observed. You can read the full press release here: https://lnkd.in/eFZkUpPz
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We are proud to support Jett Foundation's webinar: Thriving with Duchenne. This annual #RareDiseaseDay event always features incredible members of the DMD community who inspire PepGen Pioneers to work even harder to accelerate our programs.
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Meet James Gilbert, Ph.D., Scientist I, Research and Preclinical Development, here at PepGen. James plays a key role in developing and optimizing pharmacodynamic assessments across multiple PepGen programs. In addition to his technical expertise, James has participated in conferences as a presenter, where he shared updates on our EDODM1 and EDO51 efforts. His contributions play a crucial role in advancing our progress and we appreciate the opportunity to work with this Pioneer every day. To learn more about our team, visit:?https://bit.ly/48UJ8Ch?
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#TBT Last year we celebrated Rare Disease Day by reflecting on what we have learned from the rare disease community. We are looking forward to #RareDiseaseDay2025 next week!
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Rare Disease Day is only one month away, and our PepGen Pioneers cannot wait to spend the day honoring the #DMD and #DM1 communities we serve. #RareDiseaseDay #LightUpForRare
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Meet Maryanne Senn, Human Resources Business Partner, here at PepGen. With her warm presence and commitment to fostering relationships across functions, Maryanne plays a key role in driving a collaborative work environment. Maryanne's dedication to supporting both employees and the organization ensures that PepGen continues to thrive as a cohesive and values-driven team. To learn more about our team, visit:?https://bit.ly/48UJ8Ch