Dayton Children’s Hospital, clinical site for Myrtelle’s Phase 1/2 Gene Therapy Trial for Canavan Disease, created the below video that features one of our treated patients. The reel highlights the love and perseverance of this beautiful family, while eloquently telling their story and the positive outcomes they are celebrating. May this inspire further work and treatments for diseases with unmet needs.
Juan and Natalia Lavato, from Argentina, had their world changed when their son, Ciro, was diagnosed with Canavan disease, a rare degenerative condition that damages nerve cells in the brain, affecting vision, speech and motor functions. After consulting ten specialists to confirm his diagnosis, they found what mattered most to them for Ciro - hope for Ciro’s future! Ciro was accepted into a groundbreaking gene therapy clinical trial at Dayton Children's Hospital. Led by Dr. Lober, pediatric neurosurgeon at Dayton Children’s, this trial offered Ciro and his family a chance to change Ciro’s future. Ciro’s journey is a testament to the exceptional care at Dayton Children’s and the power of hope! For families like the Lavatos, Dayton Children’s isn’t just a hospital – it's a lifeline, a place where the impossible becomes possible, and where every step forward is a victory worth celebrating. ?? For more information about the gene therapy trial, visit clinicaltrials.gov. ?? Read Ciro's story: https://bit.ly/3zKUA6W #DaytonChildrensHospital #DaytonChildrens #AboveAndBeyond4Kids