Thanks to all who attended our presentations at #TLM2024 throughout the weekend. We had a great time catching up with many faces old and new, and learning about the exciting advancements in liver disease. If you would like to learn more about the data presented, visit our Publications & Presentations page. https://lnkd.in/g4d4_p39
Mirum Pharmaceuticals, Inc.
制药业
Foster City，CA 35,636 位关注者
Creating transformative medicine for people with rare liver disease.
关于我们
Mirum Pharmaceuticals, Inc. is a biopharmaceutical company dedicated to transforming the treatment of rare diseases affecting children and adults. Mirum has three approved medications: LIVMARLI? (maralixibat) oral solution, CHOLBAM? (cholic acid) capsules, and CHENODAL? (chenodiol) tablets. LIVMARLI, an IBAT inhibitor, is approved for the treatment of two rare liver diseases affecting children and adults. It is approved for the treatment of cholestatic pruritus in patients with Alagille syndrome in the U.S. (three months and older), in Europe (two months and older), and in other regions globally. It is also approved in the U.S. in cholestatic pruritus in PFIC patients five years of age and older. CHOLBAM is FDA-approved for the treatment of bile acid synthesis disorders due to single enzyme deficiencies and adjunctive treatment of peroxisomal disorders in patients who show signs or symptoms or liver disease. CHENODAL has received medical necessity recognition by the FDA to treat patients with cerebrotendinous xanthomatosis (CTX). Mirum’s late-stage pipeline includes two investigational treatments for debilitating liver diseases. Volixibat, an IBAT inhibitor, is being evaluated in two potentially registrational studies including the Phase 2b VISTAS study for primary sclerosing cholangitis and Phase 2b VANTAGE study for primary biliary cholangitis. Lastly, CHENODAL, has been evaluated in a Phase 3 clinical study, RESTORE, to treat patients with CTX, with positive topline results reported in 2023.
- 网站
-
https://mirumpharma.com/
Mirum Pharmaceuticals, Inc.的外部链接
- 所属行业
- 制药业
- 规模
- 201-500 人
- 总部
- Foster City，CA
- 类型
- 上市公司
- 创立
- 2018
地点
-
主要
获取路线
989 E Hillsdale Blvd.
Suite 300
US，CA，Foster City，94404
Mirum Pharmaceuticals, Inc.员工
动态
-
As we gear up for the final day of #TLM2024, we hope you’ll join us for Poster Session IV in Poster Hall C tomorrow from 1:00-2:00 pm PT for our late-breaker poster presentation and many more. See you there! #RareDisease
-
-
Day one of AASLD #TLM2024 has been a success! We are excited for another impactful day—join us tomorrow for an oral presentation and fireside discussion! Hope to see you there. #RareDisease
-
-
We are gearing up to attend #TLM24 AASLD The Liver Meeting ? and are honored to celebrate 75 years of AASLD alongside healthcare providers, industry colleagues, patient advocates, and many more. We look forward to seeing many of you in person and hope you’ll visit us at booth 839!
-
-
Today, we reported third quarter 2024 financial results. Tune in at 8:30 a.m. ET/5:30 a.m. PT to hear a business update from our executive team. Listen to the webcast: https://bit.ly/3Cl4Q6R Read the press release: https://bit.ly/3UOY3J7 #financialresults #thirdquarter
-
-
This #VeteransDay, we salute our country's heroes for their time and service in the US military. Today,?Benjamin M., Regional Account Manager, shares firsthand how influential his military service has been in his life, specifically in his professional life. To Ben and all our nation's veterans, THANK YOU.?
-
-
This weekend, during #NASPGHAN2024, data from our clinical studies were presented. Interested in learning more? Visit our Publications & Presentations section on mirumpharma.com to read the full analyses presented during NASPGHAN. https://bit.ly/3CgrNVx
-
-
Team Mirum has been busy at #NASPGHAN2024! It has been a phenomenal congress thus far. In case you missed it, we have five posters being presented this weekend. For details on what is being presented and when, check out our press release: https://bit.ly/4fkG99o
-
-
Team Mirum is on our way to the 2024 NASPGHAN Annual Meeting for what will surely be another meaningful and educational congress. We look forward to seeing many of you in person. Swing by and visit us at booths 401 & 301. Hope to see you there! #NASPGHAN2024
-
-
PSC Awareness Day would not be possible without the extraordinary efforts of advocates around the world partnering together to provide hope for a better future for those living with PSC. Follow our partners to learn more about PSC, their remarkable efforts, and how you can get involved! PSC PARTNERS SEEKING A CURE PSC PARTNERS SEEKING A CURE CANADA PSC Support European Liver Patients' Association - ELPA
-