Mirum Pharmaceuticals, Inc.

Mirum Pharmaceuticals, Inc.

制药业

Foster City,CA 35,637 位关注者

Creating transformative medicine for people with rare liver disease.

关于我们

Mirum Pharmaceuticals, Inc. is a biopharmaceutical company dedicated to transforming the treatment of rare diseases affecting children and adults. Mirum has three approved medications: LIVMARLI? (maralixibat) oral solution, CHOLBAM? (cholic acid) capsules, and CHENODAL? (chenodiol) tablets. LIVMARLI, an IBAT inhibitor, is approved for the treatment of two rare liver diseases affecting children and adults. It is approved for the treatment of cholestatic pruritus in patients with Alagille syndrome in the U.S. (three months and older), in Europe (two months and older), and in other regions globally. It is also approved in the U.S. in cholestatic pruritus in PFIC patients five years of age and older. CHOLBAM is FDA-approved for the treatment of bile acid synthesis disorders due to single enzyme deficiencies and adjunctive treatment of peroxisomal disorders in patients who show signs or symptoms or liver disease. CHENODAL has received medical necessity recognition by the FDA to treat patients with cerebrotendinous xanthomatosis (CTX). Mirum’s late-stage pipeline includes two investigational treatments for debilitating liver diseases. Volixibat, an IBAT inhibitor, is being evaluated in two potentially registrational studies including the Phase 2b VISTAS study for primary sclerosing cholangitis and Phase 2b VANTAGE study for primary biliary cholangitis. Lastly, CHENODAL, has been evaluated in a Phase 3 clinical study, RESTORE, to treat patients with CTX, with positive topline results reported in 2023.

网站
https://mirumpharma.com/
所属行业
制药业
规模
201-500 人
总部
Foster City,CA
类型
上市公司
创立
2018

地点

  • 主要

    989 E Hillsdale Blvd.

    Suite 300

    US,CA,Foster City,94404

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