Proud to wear our hearts on our sleeves and support the #PhelanLucky annual campaign to raise awareness of and funds for Phelan-McDermid syndrome. ?? To learn more about the campaign, visit: ·??????https://lnkd.in/e_VhFMtC ·??????https://lnkd.in/gXDfeKiZ. #22q13 #yournewfavoriteshirt #ROCKyourshamROCKS #ItsMoreThanJustAShirt #Togetherwereneveralone #PMSF #howLUCKYarewe Phelan-McDermid Syndrome Foundation
Jaguar Gene Therapy
生物技术研究
Lake Forest，IL 11,416 位关注者
Jaguar Gene Therapy is accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases.
关于我们
Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable patient populations. The company is made up of a proven team of experts with unparalleled CMC (Chemistry, Manufacturing and Controls), regulatory, clinical and commercial acumen who have first-hand experience in bringing novel gene therapy treatments to patients and their families. Committed to patient safety and product purity, Jaguar is rapidly advancing an initial pipeline of three programs targeting: 1) Type 1 galactosemia; 2) a genetic cause of autism spectrum disorder and Phelan-McDermid syndrome and other severe neurodevelopmental disorders with a SHANK3 mutation or deletion; and 3) Type 1 diabetes. The company continues to evaluate opportunities to expand its pipeline using the strength of the team and close relationships with numerous academic institutions.
- 网站
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https://www.jaguargenetherapy.com
Jaguar Gene Therapy的外部链接
- 所属行业
- 生物技术研究
- 规模
- 51-200 人
- 总部
- Lake Forest，IL
- 类型
- 私人持股
- 创立
- 2019
- 领域
- Biotechnology、Severe Genetic Diseases和Gene Therapy
地点
Jaguar Gene Therapy员工
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Andrew Knudten
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Michael DePetrillo
Scientist, Analytical Development
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Jaguar AlphA Mejia Arzayus
We Awaken, Inspire and Change Awareness. HL Films - Emerald Healing & Humanirarian Leadership &
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Shouryadeep Srivastava
MD/PhD with >14 yrs of Clinical Research experience; leading Clinical Development for exciting novel bacterial immunotherapy @Actym
动态
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We support #RareDiseaseDay and want to use this occasion to raise awareness of our partners at Phelan-McDermid Syndrome Foundation , CureSHANK and Galactosemia Foundation. We encourage you to learn more about these organizations and about Rare Disease Day.
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In recognition of Phelan-McDermid Syndrome Awareness Day, our team is raising awareness of this rare genetic condition. We encourage you to learn more from Phelan-McDermid Syndrome Foundation and consider how you can raise awareness in your community:?https://lnkd.in/d5PfxcfU.?You can also read stories about families living with Phelan-McDermid syndrome from CureSHANK:?https://lnkd.in/gZuEvnGj. #PMSAD #PMSChangesEverything #phelanmcdermidsyndrome
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Our team was excited to attend the 2024 Phelan-McDermid Syndrome Foundation Family Conference last week in Minneapolis! We appreciated meeting and talking with families about their loved ones. We also had the opportunity to present information about our JAG201 program targeting #SHANK3 haploinsufficiency. Thank you to everyone who welcomed us, listened to our presentation and shared their stories with us. To learn more about how Jaguar is accelerating breakthroughs in gene therapies for those living with severe genetic diseases, visit: www.jaguargenetherapy.com #pmsfconference2024
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This morning, we issued a press release to share updates on our JAG201 program targeting a genetic form of #autism spectrum disorder and #Phelan-McDermid syndrome. Read the full release here:?https://lnkd.in/giezNAZm #SHANK3 #phelanmcdermid
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Thanks to Michael Hughes for presenting preclinical data on our SHANK3 program at #ASGCT2024. For more information about our pipeline programs, visit: www.jaguargenetherapy.com.
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Honored to be named a “Company of the Year” by CureSHANK during their #PMSDDS last week. We are inspired by the Phelan-McDermid syndrome community and grateful for the insights and experiences they’ve shared with us. Thank you, CureSHANK, for this recognition – we are sincerely touched. #SHANK3 #phelanmcdermidsyndrome #phelanmcdermid
Congratulations to Jaguar Gene Therapy, a recipient of the CureSHANK "Company of the Year" award, presented during our inaugural PMS Drug Development Symposium (#PMSDDS) in Boston last week! Receiving the award on behalf of Jaguar were CEO Joseph Nolan and Daniel Gallo, PhD, Head of Medical Affairs. We are so thankful that Jaguar has prioritized its JAG-201 program, pioneering the first SHANK3 mini-gene replacement therapy for PMS and recently receiving an IND to begin clinical trials! The Jaguar team is a pleasure to work with and shows Jaguar's great commitment to improving patient quality of life. [These #pmsdds2024 posts are trickling in because CureSHANK is a shoestring operation with a skeleton crew mostly composed of parents caring for disabled children with PMS. To help us in our work, keep an eye out for our "Raise for Research" fundraiser, running next week May 6-10!] Pictured left to right: CureSHANK president and co-founder Geraldine Bliss; Joe Nolan; Dan Gallo. #phelanmcdermidsyndrome #phelanmcdermid #shank3 #raiseforresearch
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Yesterday, our team was happy to present an analysis that provides additional insights into the real-world burden of #galactosemia among U.S. children, adolescents and adults at the 45th Annual Meeting of the Society for Inherited Metabolic Disorders. For more information about galactosemia, visit Galactosemia Foundation: www.galactosemia.org
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April is World #Autism Month. To learn more, we encourage you to visit: https://lnkd.in/gJ2teRx.