Ionis Pharmaceuticals, Inc.

November is #NationalFamilyCaregiversMonth. Many conditions place tremendous burden not only on people living with the disease, but also on the family members who love and help care for them. We honor caregivers in our community and beyond who work tirelessly to improve lives and demonstrate radical empathy that inspires us all. Learn more and discover resources for caregivers: https://lnkd.in/e2MnMEpg

November 17th is?#InternationalERGDay, an opportunity to celebrate the employee resource groups that make our organization a stronger, more inclusive and more connected place to work. Last week, we held our annual ERG Summit, gathering more than 250 Ions to learn about our ERGs, participate in Q&As and share firsthand experiences of the benefits of joining one of our nine groups. We finished a great day of educating and recruiting new members with a learning opportunity to make our ERGs even more impactful in the year to come. Learn more about our diversity, equity and inclusion purpose:?https://lnkd.in/e_UggfRn

Recently, the?Journal of Clinical Lipidology published a manuscript about a new clinical scoring tool to facilitate diagnosis of familial chylomicronemia syndrome (FCS). FCS is a rare, genetic and difficult-to-diagnose disease that can be life threatening. Genetic testing is not always conclusive; The North American FCS (NAFCS) Score can aid in clinical evaluation and help differentiate between FCS and more common conditions with similar clinical presentation. Read the full manuscript here:?https://lnkd.in/eSPDBWNX

HCPs: Severely high triglycerides can lead to dangerous consequences. Potentially life-threating acute pancreatitis is an ever-present risk for your patients with severe hypertriglyceridemia (#sHTG) and a?genetic form, familial chylomicronemia syndrome (FCS). Better understand how to diagnose FCS and learn about dietary restrictions, medications and monitoring procedures that can help manage these debilitating diseases: https://tgaware.com/?#LivingwithFCS

Attending the 2024 Child Neurology Society Annual Meeting (#CNSAM)? Stop by booth 519 to meet members of our amazing team and learn about our latest advancements in #ChildNeurology.

This #PrionDiseaseDay, take a moment to learn about this little-understood, difficult-to-diagnose group of neurodegenerative diseases that affects about 1 in 1 million people: https://cjdisa.com/ #cjdawareness #priondiseaseawareness

Today we reported Q3 2024 financial results. Read more about our updates and tune in live to the webcast today at 11:30 AM ET to hear our third quarter highlights: https://lnkd.in/deQDzcDx

Today, we announced the pivotal Phase 3 study design for our investigational #AngelmanSyndrome (AS) medicine following alignment with the U.S. FDA. Read more: https://lnkd.in/g7azfbZw #RareDisease

The U.S. Food and Drug Administration has accepted our New Drug Application for our investigational RNA-targeted prophylactic medicine for the treatment of hereditary angioedema (#HAE) with a decision date of August 21, 2025.?? ? Read more about this milestone: https://lnkd.in/eW7GxPpk #RareDisease??

For someone #livingwithFCS (familial chylomicronemia syndrome), every meal and social event can be a challenge. Because FCS prevents the body from digesting fats and severely impairs the body’s ability to remove triglycerides from the bloodstream, consuming even small amounts of fat could trigger a trip to the emergency room.? ??? To close out #FCSAwarenessDay, watch the video to better understand how an evening out to dinner can cause anxiety for those who have FCS. To learn more, visit https://lnkd.in/egGqBYsi.??