Expression Therapeutics, Inc.转发了
Following on from the article I posted about last week on Expression Therapeutics, Inc., I would also like to share why it is important and is a breakthrough for people with/ living with people who have haemophilia A, or involved within the The Haemophilia Society Why this matters: Breakthrough in Treatment: Unlike current therapies, which often require lifelong infusions, this gene therapy has the potential to offer a one-time treatment that could eliminate the need for ongoing factor replacement. Cost and Quality of Life: Hemophilia A treatment is incredibly costly, ranging from $200,000 to $850,000 annually in the U.S. This innovative gene therapy not only promises to improve health outcomes but could also significantly reduce long-term healthcare costs. No Unexpected Safety Issues: The trial showed that the therapy was safe, with no unexpected adverse events and no development of inhibitors to Factor VIII, which can complicate treatment. For those of us living with hemophilia, this is a huge step forward. The possibility of a permanent cure gives hope for a future without the constant concern over treatment and bleeding episodes. I’m excited to see how this therapy develops and look forward to what it could mean for haemophilia patients worldwide! #Haemophilia #GeneTherapy #MedicalBreakthrough #HealthcareInnovation #Biotech #RareDisease #PatientCare #HopeForACure #LifeChangingTreatment #HaemophiliaA #FutureOfMedicine #Pharma #HealthTech #BloodDisorders #ChronicIllness #MedicalResearch