Cure GM1 Foundation

?? Every Moment Counts Children are dying when possible treatments are on the shelf. Breakthroughs happen because of supporters like you. Your support drives our work to support drug development and to attract investment. Double your impact today and help accelerate the path to treatment! Donate now: curegm1.org/donate #curegm1 #giving #hope #advocacy #nonprofit #donate

"The loss of a child is a pain that no words or actions can heal." -Unknown #curegm1 #childloss #community #grief #restinpeace

Honor all those who have lost their lives to GM1 gangliosidosis and in honor of the memories of all those gone too soon. The Compassionate Friends Worldwide Candle Lighting on the 2nd Sunday in December unites family and friends around the globe in lighting candles for one hour to honor the memories of the sons, daughters, brothers, sisters, and grandchildren who left too soon. As candles are lit on December 8th, 2024 at 7:00 pm local time, hundreds of thousands of people commemorate and honor the memory of all children gone too soon. If you would like us to recognize your loved one, please feel free to mail [email protected] #curegm1 #community #childloss #memorial #grief

You can help us make a difference to children and babies who are dying. Possible treatments are shelved. The technology and modalities exist. Don't miss our $25K matching campaign! GIVE: curegm1.org/donate #curegm1 #nevergiveup #charity #community #donate #fightforlife

Did you know that seizures require a cocktail of drugs for the majority of those impacted by GM1 gangliosidosis? FIRST AID for seizures: epilepsy.com/recognition #curegm1 #raredisease #community #epilepsy #neurology #seizures

?? This is why we're here: to shine a light on GM1 and advance possible treatments. Every single passing moment we could be closer to an approved treatment, but our progress is dependent on YOU. Don't miss our $25K matching campaign! Donate now and double your impact today - all donations matched! GIVE: curegm1.org/donate ?? Every day counts - Let's change lives now! #curegm1 #hope #advocacy #research #nonprofit #community #nevegiveup

The Ultragenyx Rare Bootcamp is an amazing experience with so much valuable information for members of the rare disease community to launch new projects and initiatives. We continue to push forward with respect to new innovative initiatives for GM1. Thank you to all the volunteers and speakers! LEARN MORE: rarebootcamp.com #curegm1 #raredisease #community #advocacy

Every day, we are working to raise awareness, fund new drug development and research projects and to advocate on behalf of the global GM1 community for the advancement of possible treatments for a fatal disease. Your support has been instrumental in making this possible, and today, we're inviting you to be part of something even bigger. Your Gift Will Go Twice as Far! curegm1.org/donate #curegm1 #hope #donate #science #advocacy #raredisease #fightforlife

We are pleased to welcome Paul to the team! BIO: Paul Fitzpatrick has nearly 30 years of biotechnology leadership experience including an impactful 20-year career at BioMarin, where he led the Biologics and Production Group, including scientific and operational responsibility for research stage biologics (ERTs) and AAV production, as well as early stage process analytics and structural, cellular, and protein biology fundamental research. Since then, Paul has worked at Zogenix, Inc. and Chameleon, Inc. doing further CMC and research work in AAV gene therapy. He now works as an independent consultant. Paul earned a Ph.D. in applied biochemistry from the Massachusetts Institute of Technology and Bachelor of Science degrees in both biology and chemistry from UC Irvine. #curegm1 #raredisease #hope #community #science

Let's continue to push for treatments and to advance our fight for life! Will you participate in our community and donate now to help us earn a $25K match by 12/3! GIVE: curegm1.org/donate #curegm1 #hope #fightforlife #raredisease #nevergiveup #charity #advocacy #nonprofit