We stand on the precipice of a historic moment. “We have the science to treat many diseases like Rose’s, but we need the regulatory and business models to do it at scale.” I’m grateful to have been invited to engage the FDA’s new Rare Disease Innovation Hub today in DC, to discuss collaborating for the future of these children and patients. I saw open and listening regulatory leaders that want to make an impact! Very exciting. I’m committed to continuing the work together. Patients, like Rose, are waiting. #platformtreatments #raredisease #aso #processapprovals #endpointrennovation
Chrysalis Genetics
生物技术研究
Austin，TX 17 位关注者
Precision medicine for children with autism and special needs
关于我们
We recognize that most children with rare genetic diseases will never see a treatment, not because the science doesn't exist, but because our system refuses to adopt a new sustainable business model. Chrysalis Genetics is a new precision medicine model for genetic treatments. We are built on the shoulder of giants like Henri Termeer, Emil Kaakis, and Dr. Tim Yu. We are born from the incredible stories of precision medicine for children, like Rose McPherson. We exist to bring treatments globally to suffering children with autism, special needs, and other neuro-genetic diseases.
- 网站
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www.chrysalisgenetics.com
Chrysalis Genetics的外部链接
- 所属行业
- 生物技术研究
- 规模
- 2-10 人
- 总部
- Austin，TX
- 类型
- 私人持股
- 创立
- 2024