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AVROBIO

AVROBIO

生物技术研究

Cambridge,Massachusetts 18,137 位关注者

Clinical-stage lentiviral gene therapy company, powered by plato?. Our vision: bring personalized gene therapy worldwide

关于我们

Our vision is to bring personalized gene therapy to the world. We target the root cause of genetic disease by introducing a functional copy of the affected gene into patients’ own hematopoietic stem cells (HSCs), with the goal of durably expressing the therapeutic protein throughout the body, including the central nervous system. Our first-in-class pipeline includes clinical programs for Gaucher disease and Hunter syndrome, as well as a preclinical program for Pompe disease. Our proprietary plato? gene therapy platform is scalable for planned global commercialization. We are headquartered in Cambridge, Mass. For additional information, visit avrobio.com, and follow us on Twitter and LinkedIn.

网站
https://www.avrobio.com
所属行业
生物技术研究
规模
51-200 人
总部
Cambridge,Massachusetts
类型
上市公司
领域
Gene Therapy和Rare Disease

地点

  • 主要

    100 Technology Sq

    6th Floor

    US,Massachusetts,Cambridge,02139

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