Alexion Pharmaceuticals, Inc.

New research from AstraZeneca in Nature Portfolio demonstrates the transformative potential for gene editing to transform outcomes for people living with rare genetic disorders by addressing their underlying causes. ? The new gene editing tool showed enhanced precision to correct genetic mutations, while reducing off-target effects. ? This advancement could help accelerate potential new treatments for a range of diseases, including rare conditions—of which 80% are believed to have a genetic cause. ? Learn more here: https://lnkd.in/eWkEhvVk

Alexion’s VP CENE Area Head Dana Vigier, MD held a compelling Fireside-Chat accompanied by Oskar Ahlberg from the Swedish patient organization Riksf?rbundet S?llsynta diagnoser - Rare Diseases Sweden at Reuters Events Pharma in London. They explored how by better understanding and improving the reality of pharma and its engagement with external stakeholders, we enable sustainable long-term partnerships that are for the benefit of patients, healthcare providers and society. The marketing continuum, particularly in orphan disease, shows that there isn’t one customer, yet the power of decision-making lies with few and doesn’t necessarily take into consideration the needs of others. They reflected on the value of inclusion and empowerment, data driven decision making and meaningful stakeholder interactions. #REcustomerEU24 #RareDisease

#RareDisease poses its own set of unique challenges for patients—this also extends to those who care for them too. But caregivers don’t have to do it alone. Check out https://spr.ly/6011uYDOv for helpful resources

Today, on October 30, we recognise #WorldHPPDay, a day dedicated to raising awareness for those living with #Hypophosphatasia (HPP). This rare, inherited, metabolic disorder can affect people of all ages. At Alexion, we’re committed to advancing research and supporting individuals, families, and their loved ones impacted by HPP. Join us in spreading awareness and knowledge about this condition to help those affected by this rare disorder.

We truly believe Alexion is a great place to work. But don’t just take our word for it – hear perspectives from a few of our very own: https://spr.ly/6042q3AgI #LifeAtAlexion

Each year on October 26, we gather with the #Amyloidosis community in honour of #WorldAmyloidosisDay to raise awareness of amyloidosis, a group of complex rare diseases caused by abnormal proteins that misfold and clump together to form amyloids that deposit in tissues or organs. Join us in showing your support for those affected by amyloidosis and their families.

Today at the World Orphan Drug Congress Europe, the rare disease advocacy community is gathered together to discuss patient-centered policies that lead to healthy health care ecosystems for rare diseases. Join Jennifer Shum and Flaminia Macchia for an informative discussion with other leaders focused on improving equitable access and care for people living with rare diseases across Europe and around the world. #Alexion #WODCEurope2024

The World Orphan Drug Congress Europe 2024 is ongoing in Barcelona, a city that is home to our AstraZeneca Global Hub with a strong scientific focus on developing innovative therapies for rare diseases. We’re thrilled to bridge Spain’s significant life science innovation engine with the unmet needs of people living with rare diseases, here and around the world. Come find us at our booth and learn more. #Alexion #WODCEurope2024

"When it comes to health care for people living with rare diseases, we have a collective responsibility to leave no one behind, to ensure patients have equal opportunities to access health care that works for them. We must have more people screened and diagnosed earlier in their health journey. More people with options for more clinical trials. More people with access to the best possible treatments and coordinated care, no matter where they live.” Hear more from Soraya Bekkali, MD at the World Orphan Drug Congress Europe in her Keynote address, opening this keystone congress for the rare disease community in Barcelona, starting tomorrow. #Alexion #WODCEurope2024

At Alexion, we're not just hiring employees; we're building a team of passionate individuals committed to making a real difference for the #RareDisease community. Hear from a few of our colleagues what makes #LifeAtAlexion so special. ?